Reconstructing the Rasch-Built Myotonic Dystrophy Type 1 Activity and Participation Scale

PLoS One. 2015 Oct 20;10(10):e0139944. doi: 10.1371/journal.pone.0139944. eCollection 2015.

Abstract

Introduction: A previously published Rasch-built activity and participation scale specifically designed for patients with myotonic dystrophy type 1 (DM1) was criticized for having been constructed in a relatively small cohort of patients and containing items too broadly phrased for DM1 patients, thus hampering its clinical use.

Methods: We report the results of the reconstructed Rasch-built DM1 activity and participation scale for clinical use (DM1-ActivC) through Rasch analyses using an expanded questionnaire containing 146 more simply phrased activity and participation inquiries completed by 340 patients with DM1.

Results: Through stepwise investigation including data quality control, model fit, response category ordering, local dependency and item bias, we succeeded in reconstructing the DM1-ActivC consisting of 25 items that showed good Rasch model fit, including construct convergent validity, items' weights and persons' locations reliability, and unidimensionality.

Conclusion: The DM1-ActivC scale has been reconstructed and fulfills all modern clinimetric requirements. Its use is recommended in future longitudinal trials in patients with DM1 to determine its responsiveness.

Publication types

  • Validation Study

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Aged, 80 and over
  • Disability Evaluation*
  • Female
  • Humans
  • Male
  • Middle Aged
  • Motor Activity / physiology*
  • Myotonic Dystrophy / diagnosis
  • Myotonic Dystrophy / physiopathology*
  • Psychometrics
  • Reproducibility of Results
  • Severity of Illness Index
  • Surveys and Questionnaires
  • Young Adult

Grants and funding

The authors have no support or funding to report.