Heterozygous deletion of the LRFN2 gene is associated with working memory deficits

Eur J Hum Genet. 2016 Jun;24(6):911-8. doi: 10.1038/ejhg.2015.221. Epub 2015 Oct 21.

Abstract

Learning disabilities (LDs) are a clinically and genetically heterogeneous group of diseases. Array-CGH and high-throughput sequencing have dramatically expanded the number of genes implicated in isolated intellectual disabilities and LDs, highlighting the implication of neuron-specific post-mitotic transcription factors and synaptic proteins as candidate genes. We report a unique family diagnosed with autosomal dominant learning disability and a 6p21 microdeletion segregating in three patients. The 870 kb microdeletion encompassed the brain-expressed gene LRFN2, which encodes for a synaptic cell adhesion molecule. Neuropsychological assessment identified selective working memory deficits, with borderline intellectual functioning. Further investigations identified a defect in executive function, and auditory-verbal processes. These data were consistent with brain MRI and FDG-PET functional brain imaging, which, when compared with controls, revealed abnormal brain volume and hypometabolism of gray matter structures implicated in working memory. We performed electron microscopy immunogold labeling demonstrating the localization of LRFN2 at synapses of cerebellar and hippocampal rat neurons, often associated with the NR1 subunit of N-methyl-D-aspartate receptors (NMDARs). Altogether, the combined approaches imply a role for LRFN2 in LD, specifically for working memory processes and executive function. In conclusion, the identification of familial cases of clinically homogeneous endophenotypes of LD might help in both the management of patients and genetic counseling for families.

MeSH terms

  • Adult
  • Animals
  • Brain / diagnostic imaging
  • Cells, Cultured
  • Child
  • Female
  • Fluorodeoxyglucose F18
  • Gene Deletion*
  • Heterozygote
  • Humans
  • Learning Disabilities / complications
  • Learning Disabilities / diagnosis
  • Learning Disabilities / genetics*
  • Magnetic Resonance Imaging
  • Male
  • Membrane Glycoproteins
  • Membrane Proteins / genetics*
  • Membrane Proteins / metabolism
  • Memory Disorders / complications
  • Memory Disorders / diagnosis
  • Memory Disorders / genetics*
  • Memory, Short-Term*
  • Nerve Tissue Proteins
  • Pedigree
  • Positron-Emission Tomography
  • Radiopharmaceuticals
  • Rats
  • Rats, Sprague-Dawley
  • Receptors, N-Methyl-D-Aspartate / metabolism
  • Synapses / metabolism
  • Synapses / ultrastructure

Substances

  • LRFN2 protein, human
  • Membrane Glycoproteins
  • Membrane Proteins
  • Nerve Tissue Proteins
  • Radiopharmaceuticals
  • Receptors, N-Methyl-D-Aspartate
  • Fluorodeoxyglucose F18