Transfusion and Treatment of severe anaemia in African children (TRACT): a study protocol for a randomised controlled trial

Trials. 2015 Dec 29:16:593. doi: 10.1186/s13063-015-1112-4.

Abstract

Background: In sub-Saharan Africa, where infectious diseases and nutritional deficiencies are common, severe anaemia is a common cause of paediatric hospital admission, yet the evidence to support current treatment recommendations is limited. To avert overuse of blood products, the World Health Organisation advocates a conservative transfusion policy and recommends iron, folate and anti-helminthics at discharge. Outcomes are unsatisfactory with high rates of in-hospital mortality (9-10%), 6-month mortality and relapse (6%). A definitive trial to establish best transfusion and treatment strategies to prevent both early and delayed mortality and relapse is warranted.

Methods/design: TRACT is a multicentre randomised controlled trial of 3954 children aged 2 months to 12 years admitted to hospital with severe anaemia (haemoglobin < 6 g/dl). Children will be enrolled over 2 years in 4 centres in Uganda and Malawi and followed for 6 months. The trial will simultaneously evaluate (in a factorial trial with a 3 x 2 x 2 design) 3 ways to reduce short-term and longer-term mortality and morbidity following admission to hospital with severe anaemia in African children. The trial will compare: (i) R1: liberal transfusion (30 ml/kg whole blood) versus conservative transfusion (20 ml/kg) versus no transfusion (control). The control is only for children with uncomplicated severe anaemia (haemoglobin 4-6 g/dl); (ii) R2: post-discharge multi-vitamin multi-mineral supplementation (including folate and iron) versus routine care (folate and iron) for 3 months; (iii) R3: post-discharge cotrimoxazole prophylaxis for 3 months versus no prophylaxis. All randomisations are open. Enrolment to the trial started September 2014 and is currently ongoing. Primary outcome is cumulative mortality to 4 weeks for the transfusion strategy comparisons, and to 6 months for the nutritional support/antibiotic prophylaxis comparisons. Secondary outcomes include mortality, morbidity (haematological correction, nutritional and infectious), safety and cost-effectiveness.

Discussion: If confirmed by the trial, a cheap and widely available 'bundle' of effective interventions, directed at immediate and downstream consequences of severe anaemia, could lead to substantial reductions in mortality in a substantial number of African children hospitalised with severe anaemia every year, if widely implemented.

Trial registration: Current Controlled Trials ISRCTN84086586 , Approved 11 February 2013.

Publication types

  • Multicenter Study
  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Age Factors
  • Anemia / blood
  • Anemia / diagnosis
  • Anemia / mortality
  • Anemia / therapy*
  • Anthelmintics / administration & dosage
  • Biomarkers / blood
  • Blood Transfusion* / mortality
  • Child
  • Child Mortality
  • Child, Preschool
  • Clinical Protocols
  • Dietary Supplements
  • Drug Administration Schedule
  • Health Status
  • Hemoglobins / metabolism
  • Hospital Mortality
  • Humans
  • Infant
  • Infant Mortality
  • Malawi
  • Nutritional Status
  • Patient Admission
  • Recurrence
  • Research Design
  • Risk Factors
  • Severity of Illness Index
  • Time Factors
  • Transfusion Reaction
  • Treatment Outcome
  • Trimethoprim, Sulfamethoxazole Drug Combination / administration & dosage
  • Uganda
  • Vitamins / administration & dosage

Substances

  • Anthelmintics
  • Biomarkers
  • Hemoglobins
  • Vitamins
  • Trimethoprim, Sulfamethoxazole Drug Combination

Associated data

  • ISRCTN/ISRCTN84086586