Recombinant human pentraxin-2 therapy in patients with idiopathic pulmonary fibrosis: safety, pharmacokinetics and exploratory efficacy

Eur Respir J. 2016 Mar;47(3):889-97. doi: 10.1183/13993003.00850-2015. Epub 2016 Feb 11.

Abstract

Abnormal fibrogenic repair response upon alveolar injury is believed to play an important role in the pathogenesis of idiopathic pulmonary fibrosis (IPF). PRM-151 (recombinant human pentraxin-2, also known as serum amyloid P), has been shown to reduce fibrosis in preclinical lung fibrosis models, and was well tolerated with a favourable pharmacokinetic profile in an earlier single-dose phase I study.A randomised, double-blind, placebo-controlled, multiple ascending dose trial was performed to assess the tolerability and pharmacokinetic and pharmacodynamic characteristics of multiple doses of PRM-151 in IPF patients. Subjects in three successive cohorts (1, 5, or 10 mg·kg(-1) versus placebo) received intravenous study drug on days 1, 3, 5, 8 and 15, and were followed-up to day 57.PRM-151 was well tolerated at all dose levels, with no serious adverse reactions. Administration of PRM-151 resulted in two- to eight-fold dose-dependent increases in circulating pentraxin-2 levels. Forced vital capacity and 6-min walk test showed trends towards improvement in the combined PRM-151 dose groups. On high-resolution computed tomography scans, stable or improved lung volume unoccupied by interstitial lung abnormality was noted in some PRM-151 subjects compared to placebo subjects on day 57.The efficacy of PRM-151 in IPF remains to be investigated in dedicated future trials.

Trial registration: ClinicalTrials.gov NCT01254409.

Publication types

  • Multicenter Study
  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Dose-Response Relationship, Drug
  • Double-Blind Method
  • Exercise Test
  • Female
  • Homeodomain Proteins / adverse effects
  • Homeodomain Proteins / pharmacokinetics*
  • Humans
  • Idiopathic Pulmonary Fibrosis / drug therapy*
  • Lung / physiopathology*
  • Male
  • Middle Aged
  • Netherlands
  • Recombinant Proteins / adverse effects
  • Recombinant Proteins / pharmacokinetics
  • Respiratory Function Tests
  • Serum Amyloid P-Component / adverse effects
  • Serum Amyloid P-Component / pharmacokinetics*
  • Treatment Outcome
  • United States

Substances

  • Homeodomain Proteins
  • PRM-151
  • Recombinant Proteins
  • Serum Amyloid P-Component

Associated data

  • ClinicalTrials.gov/NCT01254409