Serum Levels of Progranulin Do Not Reflect Cerebrospinal Fluid Levels in Neurodegenerative Disease

Curr Alzheimer Res. 2016;13(6):654-62. doi: 10.2174/1567205013666160314151247.

Abstract

Altered progranulin levels play a major role in neurodegenerative diseases, like Alzheimer's dementia (AD), frontotemporal dementia (FTD) and amyotrophic lateral sclerosis (ALS), even in the absence of GRN mutations. Increasing progranulin levels could hereby provide a novel treatment strategy. However, knowledge on progranulin regulation in neurodegenerative diseases remains limited. We here demonstrate that cerebrospinal fluid progranulin levels do not correlate with its serum levels in AD, FTD and ALS, indicating a differential regulation of its central and peripheral levels in neurodegeneration. Blood progranulin levels thus do not reliably predict central nervous progranulin levels and their response to future progranulin-increasing therapeutics.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aged
  • Alzheimer Disease / genetics
  • Alzheimer Disease / metabolism*
  • Amyotrophic Lateral Sclerosis / genetics
  • Amyotrophic Lateral Sclerosis / metabolism*
  • Biomarkers / blood
  • Biomarkers / cerebrospinal fluid
  • Female
  • Frontotemporal Dementia / genetics
  • Frontotemporal Dementia / metabolism*
  • Humans
  • Intercellular Signaling Peptides and Proteins / blood*
  • Intercellular Signaling Peptides and Proteins / cerebrospinal fluid*
  • Intercellular Signaling Peptides and Proteins / genetics
  • Male
  • Middle Aged
  • Progranulins

Substances

  • Biomarkers
  • GRN protein, human
  • Intercellular Signaling Peptides and Proteins
  • Progranulins