Structure of the Human Protein Kinase ZAK in Complex with Vemurafenib

ACS Chem Biol. 2016 Jun 17;11(6):1595-602. doi: 10.1021/acschembio.6b00043. Epub 2016 Mar 31.

Abstract

The mixed lineage kinase ZAK is a key regulator of the MAPK pathway mediating cell survival and inflammatory response. ZAK is targeted by several clinically approved kinase inhibitors, and inhibition of ZAK has been reported to protect from doxorubicin-induced cardiomyopathy. On the other hand, unintended targeting of ZAK has been linked to severe adverse effects such as the development of cutaneous squamous cell carcinoma. Therefore, both specific inhibitors of ZAK, as well as anticancer drugs lacking off-target activity against ZAK, may provide therapeutic benefit. Here, we report the first crystal structure of ZAK in complex with the B-RAF inhibitor vemurafenib. The cocrystal structure displayed a number of ZAK-specific features including a highly distorted P loop conformation enabling rational inhibitor design. Positional scanning peptide library analysis revealed a unique substrate specificity of the ZAK kinase including unprecedented preferences for histidine residues at positions -1 and +2 relative to the phosphoacceptor site. In addition, we screened a library of clinical kinase inhibitors identifying several inhibitors that potently inhibit ZAK, demonstrating that this kinase is commonly mistargeted by currently used anticancer drugs.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenosine Triphosphate / analogs & derivatives
  • Adenosine Triphosphate / chemistry
  • Calorimetry
  • Crystallography, X-Ray
  • Drug Design
  • Humans
  • Indoles / chemistry*
  • Leucine Zippers
  • MAP Kinase Kinase Kinases
  • Molecular Structure
  • Oligopeptides / chemical synthesis
  • Oligopeptides / chemistry
  • Phosphoproteins / chemistry
  • Phosphorylation
  • Protein Kinase Inhibitors / chemistry*
  • Protein Kinases / chemistry*
  • Proto-Oncogene Proteins B-raf / antagonists & inhibitors
  • Proto-Oncogene Proteins B-raf / chemistry
  • Sulfonamides / chemistry*
  • Vemurafenib

Substances

  • Indoles
  • Oligopeptides
  • Phosphoproteins
  • Protein Kinase Inhibitors
  • Sulfonamides
  • Vemurafenib
  • adenosine 5'-O-(3-thiotriphosphate)
  • Adenosine Triphosphate
  • Protein Kinases
  • Proto-Oncogene Proteins B-raf
  • MAP Kinase Kinase Kinases
  • MAP3K20 protein, human