Efficacy of hematopoietic cell transplantation in metachromatic leukodystrophy: the Dutch experience

Blood. 2016 Jun 16;127(24):3098-101. doi: 10.1182/blood-2016-03-708479. Epub 2016 Apr 26.
No abstract available

Publication types

  • Letter
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Child
  • Child, Preschool
  • Cognition
  • Cohort Studies
  • Hematopoietic Stem Cell Transplantation*
  • Humans
  • Leukodystrophy, Metachromatic / epidemiology
  • Leukodystrophy, Metachromatic / physiopathology
  • Leukodystrophy, Metachromatic / therapy*
  • Netherlands / epidemiology
  • Survival Analysis
  • Treatment Outcome
  • Young Adult