Background and purpose: Disease severity varies considerably among patients with Spinal and Bulbar Muscular Atrophy (SBMA). Our aim was to investigate the role of androgen receptor (AR) polymorphic repeats in SBMA phenotype.
Methods: We analyzed the length of AR polyQ and polyG tracts in 159 SBMA patients.
Results: No relationship between polyG size or polyG/polyQ haplotypes and clinical phenotype was found. An independent negative correlation between polyQ-length and onset of weakness was confirmed (P < 0.001).
Conclusions: The negative results of our study prompt to continue the search for potential disease modifiers in SBMA outside the AR gene.
Keywords: genotype; phenotype; polyG; polyQ; spinal and bulbar muscular atrophy.
© 2016 EAN.