Pioglitazone Enhances the Beneficial Effects of Glucocorticoids in Experimental Nephrotic Syndrome

Sci Rep. 2016 May 4:6:24392. doi: 10.1038/srep24392.

Abstract

Glucocorticoids are the primary therapy for nephrotic syndrome (NS), but have serious side effects and are ineffective in ~20-50% of patients. Thiazolidinediones have recently been suggested to be renoprotective, and to modulate podocyte glucocorticoid-mediated nuclear receptor signaling. We hypothesized that thiazolidinediones could enhance glucocorticoid efficacy in NS. We found that puromycin aminonucleoside-induced proteinuria in rats was significantly reduced by both high-dose glucocorticoids (79%) and pioglitazone (61%), but not low-dose glucocorticoids (25%). Remarkably, pioglitazone + low-dose glucocorticoids also reduced proteinuria (63%) comparably to high-dose glucocorticoids, whereas pioglitazone + high-dose glucocorticoids reduced proteinuria to almost control levels (97%). Molecular analysis revealed that both glucocorticoids and pioglitazone enhanced glomerular synaptopodin and nephrin expression, and reduced COX-2 expression, after injury. Furthermore, the glomerular phosphorylation of glucocorticoid receptor and Akt, but not PPARγ, correlated with treatment-induced reductions in proteinuria. Notably, clinical translation of these findings to a child with refractory NS by the addition of pioglitazone to the treatment correlated with marked reductions in both proteinuria (80%) and overall immunosuppression (64%). These findings together suggest that repurposing pioglitazone could potentially enhance the proteinuria-reducing effects of glucocorticoids during NS treatment.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Albuminuria / etiology
  • Animals
  • Creatinine / urine
  • Cyclooxygenase 2 / genetics
  • Cyclooxygenase 2 / metabolism
  • Drug Therapy, Combination
  • Glucocorticoids / adverse effects
  • Glucocorticoids / pharmacology
  • Glucocorticoids / therapeutic use*
  • Kidney Glomerulus / drug effects
  • Kidney Glomerulus / metabolism
  • Kidney Glomerulus / pathology
  • Male
  • Membrane Proteins / genetics
  • Membrane Proteins / metabolism
  • Microfilament Proteins / genetics
  • Microfilament Proteins / metabolism
  • Nephrotic Syndrome / chemically induced
  • Nephrotic Syndrome / drug therapy*
  • Nephrotic Syndrome / pathology
  • PPAR gamma / metabolism
  • Phosphorylation / drug effects
  • Pioglitazone
  • Proteinuria / etiology
  • Puromycin Aminonucleoside / toxicity
  • Rats
  • Rats, Wistar
  • Signal Transduction / drug effects
  • Thiazolidinediones / pharmacology
  • Thiazolidinediones / therapeutic use*
  • Urinalysis

Substances

  • Glucocorticoids
  • Membrane Proteins
  • Microfilament Proteins
  • PPAR gamma
  • Synpo protein, rat
  • Thiazolidinediones
  • nephrin
  • Puromycin Aminonucleoside
  • Creatinine
  • Cyclooxygenase 2
  • Pioglitazone