Systematic drug screening reveals specific vulnerabilities and co-resistance patterns in endocrine-resistant breast cancer

BMC Cancer. 2016 Jul 4:16:378. doi: 10.1186/s12885-016-2452-5.

Abstract

Background: The estrogen receptor (ER) inhibitor tamoxifen reduces breast cancer mortality by 31 % and has served as the standard treatment for ER-positive breast cancers for decades. However, 50 % of advanced ER-positive cancers display de novo resistance to tamoxifen, and acquired resistance evolves in 40 % of patients who initially respond. Mechanisms underlying resistance development remain poorly understood and new therapeutic opportunities are urgently needed. Here, we report the generation and characterization of seven tamoxifen-resistant breast cancer cell lines from four parental strains.

Methods: Using high throughput drug sensitivity and resistance testing (DSRT) with 279 approved and investigational oncology drugs, exome-sequencing and network analysis, we for the first time, systematically determine the drug response profiles specific to tamoxifen resistance.

Results: We discovered emerging vulnerabilities towards specific drugs, such as ERK1/2-, proteasome- and BCL-family inhibitors as the cells became tamoxifen-resistant. Co-resistance to other drugs such as the survivin inhibitor YM155 and the chemotherapeutic agent paclitaxel also occurred.

Conclusion: This study indicates that multiple molecular mechanisms dictate endocrine resistance, resulting in unexpected vulnerabilities to initially ineffective drugs, as well as in emerging co-resistances. Thus, combatting drug-resistant tumors will require patient-tailored strategies in order to identify new drug vulnerabilities, and to understand the associated co-resistance patterns.

Keywords: Breast cancer; Drug resistance; Exome-sequencing; High-throughput drug testing; Tamoxifen resistance.

MeSH terms

  • Breast Neoplasms / genetics*
  • Cell Line, Tumor
  • Drug Resistance, Multiple*
  • Drug Resistance, Neoplasm*
  • Drug Screening Assays, Antitumor
  • Drugs, Investigational
  • Exome
  • Female
  • Gene Expression Regulation, Neoplastic / drug effects
  • Gene Regulatory Networks / drug effects*
  • Genomic Instability
  • High-Throughput Screening Assays / methods
  • Humans
  • Imidazoles / pharmacology
  • MCF-7 Cells
  • Naphthoquinones / pharmacology
  • Paclitaxel / pharmacology
  • Sequence Analysis, DNA / methods
  • Small Molecule Libraries / pharmacology*
  • Tamoxifen / pharmacology*

Substances

  • Drugs, Investigational
  • Imidazoles
  • Naphthoquinones
  • Small Molecule Libraries
  • Tamoxifen
  • Paclitaxel
  • sepantronium