Mutations in glucocerebrosidase are a major genetic risk factor for Parkinson's disease and increase susceptibility to dementia in a Flanders-Belgian cohort

Neurosci Lett. 2016 Aug 26:629:160-164. doi: 10.1016/j.neulet.2016.07.008. Epub 2016 Jul 7.

Abstract

Objective: To investigate the frequency of glucocerebrosidase (GBA) mutations in a Flanders-Belgian Parkinson's disease (PD) patient cohort and to assess genotype-phenotype correlations.

Methods: We performed an in-depth sequencing of all coding exons of GBA in 266 clinically well-characterized PD patients and 536 healthy control individuals.

Results: We identified rare, heterozygous GBA mutations in 12 PD patients (4.5%) and in 2 healthy control individuals (0.37%), confirming the genetic association of GBA mutations with PD in the Flanders-Belgian population (p<0.001). The patient carriers had a more severe Unified Parkinson's Disease Rating Scale (UPDRS) motor score than non-carriers. Also, GBA mutation status was a significant, independent predictor for the presence of dementia (OR=12.43, 95% CI: 2.27-68.14. p=0.004). Genetic association of PD with the common p.E326K and p.T369M variants in GBA was absent.

Conclusion: In our Flanders-Belgian cohort, carrier status of a heterozygous GBA mutation was a strong genetic risk factor for PD. The GBA mutation frequency of 4.5% is comparable to previously reported data in other European PD patient cohorts. Furthermore, our clinical data suggest a more severe motor phenotype and a strong predisposition to dementia in GBA mutation carriers.

Keywords: GBA; Genotype-phenotype correlation; Glucocerebrosidase; Parkinson’s disease.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aged
  • Belgium
  • Cohort Studies
  • Dementia / complications
  • Dementia / genetics*
  • Exons
  • Female
  • Genetic Association Studies
  • Genetic Predisposition to Disease*
  • Glucosylceramidase / genetics*
  • Heterozygote
  • Humans
  • Male
  • Middle Aged
  • Mutation
  • Parkinson Disease / complications
  • Parkinson Disease / genetics*
  • Phenotype
  • Risk Factors
  • Severity of Illness Index

Substances

  • Glucosylceramidase