The efficient elimination of solid tumor cells by EGFR-specific and HER2-specific scFv-SNAP fusion proteins conjugated to benzylguanine-modified auristatin F

Cancer Lett. 2016 Oct 28;381(2):323-30. doi: 10.1016/j.canlet.2016.08.003. Epub 2016 Aug 5.

Abstract

Antibody-drug conjugates (ADCs) combine the potency of cytotoxic drugs with the specificity of monoclonal antibodies (mAbs). Most ADCs are currently generated by the nonspecific conjugation of drug-linker reagents to certain amino acid residues in mAbs, resulting in a heterogeneous product. To overcome this limitation and prepare ADCs with a defined stoichiometry, we use SNAP-tag technology as an alternative conjugation strategy. This allows the site-specific conjugation of O(6)-benzylguanine (BG)-modified small molecules to SNAP-tag fusion proteins. To demonstrate the suitability of this system for the preparation of novel recombinant ADCs, here we conjugated SNAP-tagged single chain antibody fragments (scFvs) to a BG-modified version of auristatin F (AURIF). We used two scFv-SNAP fusion proteins targeting members of the epidermal growth factor receptor (EGFR) family that are frequently overexpressed in breast cancer. The conjugation of BG-AURIF to EGFR-specific 425(scFv)-SNAP and HER2-specific αHER2(scFv)-SNAP resulted in two potent recombinant ADCs that specifically killed breast cancer cell lines by inducing apoptosis when applied at nanomolar concentrations. These data confirm that SNAP-tag technology is a promising tool for the generation of novel recombinant ADCs.

Keywords: ADC; Auristatin; EGFR; HER2; SNAP-tag technology.

MeSH terms

  • Animals
  • Antineoplastic Agents / pharmacology*
  • Apoptosis / drug effects
  • Breast Neoplasms / drug therapy*
  • Breast Neoplasms / immunology
  • Breast Neoplasms / metabolism
  • Breast Neoplasms / pathology
  • Cell Cycle Checkpoints / drug effects
  • Cell Line, Tumor
  • Cell Survival / drug effects
  • Dose-Response Relationship, Drug
  • Drug Stability
  • ErbB Receptors / immunology*
  • ErbB Receptors / metabolism
  • Guanine / analogs & derivatives*
  • Guanine / pharmacology
  • Humans
  • Immunotherapy / methods*
  • Immunotoxins / immunology
  • Immunotoxins / pharmacology*
  • Inhibitory Concentration 50
  • Mice
  • Oligopeptides / pharmacology*
  • Q-SNARE Proteins / immunology
  • Q-SNARE Proteins / pharmacology*
  • Receptor, ErbB-2 / immunology*
  • Receptor, ErbB-2 / metabolism
  • Recombinant Fusion Proteins / pharmacology
  • Signal Transduction / drug effects
  • Single-Chain Antibodies / immunology
  • Single-Chain Antibodies / pharmacology*

Substances

  • Antineoplastic Agents
  • Immunotoxins
  • Oligopeptides
  • Q-SNARE Proteins
  • Recombinant Fusion Proteins
  • Single-Chain Antibodies
  • Guanine
  • EGFR protein, human
  • EGFR protein, mouse
  • ERBB2 protein, human
  • ErbB Receptors
  • Erbb2 protein, mouse
  • Receptor, ErbB-2