Integrated Approach to Identify Heparan Sulfate Ligand Requirements of Robo1

J Am Chem Soc. 2016 Oct 5;138(39):13059-13067. doi: 10.1021/jacs.6b08161. Epub 2016 Sep 27.

Abstract

An integrated methodology is described to establish ligand requirements for heparan sulfate (HS) binding proteins based on a workflow in which HS octasaccharides are produced by partial enzymatic degradation of natural HS followed by size exclusion purification, affinity enrichment using an immobilized HS-binding protein of interest, putative structure determination of isolated compounds by a hydrophilic interaction chromatography-high-resolution mass spectrometry platform, and chemical synthesis of well-defined HS oligosaccharides for structure-activity relationship studies. The methodology was used to establish the ligand requirements of human Roundabout receptor 1 (Robo1), which is involved in a number of developmental processes. Mass spectrometric analysis of the starting octasaccharide mixture and the Robo1-bound fraction indicated that Robo1 has a preference for a specific set of structures. Further analysis was performed by sequential permethylation, desulfation, and pertrideuteroacetylation followed by online separation and structural analysis by MS/MS. Sequences of tetrasaccharides could be deduced from the data, and by combining the compositional and sequence data, a putative octasaccharide ligand could be proposed (GlA-GlcNS6S-IdoA-GlcNS-IdoA2S-GlcNS6S-IdoA-GlcNAc6S). A modular synthetic approach was employed to prepare the target compound, and binding studies by surface plasmon resonance (SPR) confirmed it to be a high affinity ligand for Robo1. Further studies with a number of tetrasaccharides confirmed that sulfate esters at C-6 are critical for binding, whereas such functionalities at C-2 substantially reduce binding. High affinity ligands were able to reverse a reduction in endothelial cell migration induced by Slit2-Robo1 signaling.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Cell Movement
  • Heparitin Sulfate / metabolism*
  • Humans
  • Ligands
  • Nerve Tissue Proteins / metabolism*
  • Protein Binding
  • Receptors, Immunologic / metabolism*
  • Roundabout Proteins

Substances

  • Ligands
  • Nerve Tissue Proteins
  • Receptors, Immunologic
  • Heparitin Sulfate