Fabry disease: A pharmacological chaperone on the horizon

Nat Rev Nephrol. 2016 Nov;12(11):653-654. doi: 10.1038/nrneph.2016.138. Epub 2016 Sep 26.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't
  • Comment

MeSH terms

  • 1-Deoxynojirimycin / analogs & derivatives
  • Fabry Disease*
  • Humans
  • Molecular Chaperones

Substances

  • Molecular Chaperones
  • 1-Deoxynojirimycin
  • migalastat