Systematic mapping of functional enhancer-promoter connections with CRISPR interference

Science. 2016 Nov 11;354(6313):769-773. doi: 10.1126/science.aag2445. Epub 2016 Sep 29.

Abstract

Gene expression in mammals is regulated by noncoding elements that can affect physiology and disease, yet the functions and target genes of most noncoding elements remain unknown. We present a high-throughput approach that uses clustered regularly interspaced short palindromic repeats (CRISPR) interference (CRISPRi) to discover regulatory elements and identify their target genes. We assess >1 megabase of sequence in the vicinity of two essential transcription factors, MYC and GATA1, and identify nine distal enhancers that control gene expression and cellular proliferation. Quantitative features of chromatin state and chromosome conformation distinguish the seven enhancers that regulate MYC from other elements that do not, suggesting a strategy for predicting enhancer-promoter connectivity. This CRISPRi-based approach can be applied to dissect transcriptional networks and interpret the contributions of noncoding genetic variation to human disease.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • CRISPR-Cas Systems
  • Cell Proliferation / genetics
  • Chromosome Mapping / methods*
  • Clustered Regularly Interspaced Short Palindromic Repeats*
  • Disease / genetics
  • Enhancer Elements, Genetic / genetics
  • Enhancer Elements, Genetic / physiology*
  • GATA1 Transcription Factor / genetics
  • Gene Expression Regulation
  • High-Throughput Nucleotide Sequencing / methods*
  • Humans
  • K562 Cells
  • Promoter Regions, Genetic / genetics
  • Promoter Regions, Genetic / physiology*
  • Proto-Oncogene Proteins c-myc / genetics
  • Real-Time Polymerase Chain Reaction

Substances

  • GATA1 Transcription Factor
  • GATA1 protein, human
  • MYC protein, human
  • Proto-Oncogene Proteins c-myc