A Phase 4 Prospective Study in Patients with Adult Pompe Disease Treated with Alglucosidase Alfa

Affiliations

• ¹ Genzyme, a Sanofi Company, Cambridge, MA, USA.
• ² Institut de Myologie, NMR Laboratory - Spectroscopy Laboratory, Université Pierre et Marie Curie, Paris, France.
• ³ Department of Neurology, Division of Neuromuscular Medicine, Ohio State University Wexner Medical Center, Columbus, OH, USA.
• ⁴ Friedrich-Baur Institut, Neurologische Klinik, Klinikum der Universität München, Munich, Germany.
• ⁵ Neuroscience Center, Center for Advanced Medicine, St. Louis, MO, USA.
• ⁶ Department of Neurology, University of Kansas Medical Center, Kansas City, KS, USA.
• ⁷ Lysosomal Disorders Unit and Center for Clinical Trials, O&O Alpan LLC, Fairfax, VA, USA.
• ⁸ Department of Neurology, University of California, Irvine, Irvine, CA, USA.
• ⁹ Division of Pediatric Medical Genetics, Duke University Medical Center, Durham, NC, USA.
• ¹⁰ Penn State Hershey Neurology, Hershey, PA, USA.
• ¹¹ Institute of Genetic Medicine, Newcastle University, Newcastle upon Tyne, UK.
• ¹² Department of Sleep Medicine and Neuromuscular Disorders, University Hospital of Münster, Münster, Germany.
• ¹³ Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.