Topical tacrolimus for the treatment of secondary lymphedema

Nat Commun. 2017 Feb 10:8:14345. doi: 10.1038/ncomms14345.

Abstract

Secondary lymphedema, a life-long complication of cancer treatment, currently has no cure. Lymphedema patients have decreased quality of life and recurrent infections with treatments limited to palliative measures. Accumulating evidence indicates that T cells play a key role in the pathology of lymphedema by promoting tissue fibrosis and inhibiting lymphangiogenesis. Here using mouse models, we show that topical therapy with tacrolimus, an anti-T-cell immunosuppressive drug, is highly effective in preventing lymphedema development and treating established lymphedema. This intervention markedly decreases swelling, T-cell infiltration and tissue fibrosis while significantly increasing formation of lymphatic collaterals with minimal systemic absorption. Animals treated with tacrolimus have markedly improved lymphatic function with increased collecting vessel contraction frequency and decreased dermal backflow. These results have profound implications for lymphedema treatment as topical tacrolimus is FDA-approved for other chronic skin conditions and has an established record of safety and tolerability.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Disease Models, Animal*
  • Endothelial Cells / drug effects
  • Endothelial Cells / pathology
  • Female
  • Fibrosis / prevention & control
  • Humans
  • Immunosuppressive Agents / administration & dosage
  • Immunosuppressive Agents / pharmacology
  • Lymph Node Excision / adverse effects
  • Lymphatic Vessels / drug effects*
  • Lymphatic Vessels / pathology
  • Lymphedema / drug therapy
  • Mice, Inbred C57BL
  • T-Lymphocytes / drug effects
  • T-Lymphocytes / pathology
  • Tacrolimus / administration & dosage
  • Tacrolimus / pharmacology*
  • Treatment Outcome

Substances

  • Immunosuppressive Agents
  • Tacrolimus