Autosomal dominant cutis laxa with progeroid features due to a novel, de novo mutation in ALDH18A1

J Hum Genet. 2017 Jun;62(6):661-663. doi: 10.1038/jhg.2017.18. Epub 2017 Feb 23.

Abstract

De novo dominant mutations in the aldehyde dehydrogenase 18 family member A1 (ALDH18A1) gene have recently been shown to cause autosomal dominant cutis laxa with progeroid features (MIM 616603). To date, all de novo dominant mutations have been found in a single highly conserved amino acid residue at position p.Arg138. We report an 8-year-old male with a clinical diagnosis of autosomal dominant cutis laxa (ADCL) with progeroid features and a novel de novo missense mutation in ALDH18A1 (NM_002860.3: c.377G>A (p.Arg126His)). This is the first report of an individual with ALDH18A1-ADCL due to a substitution at a residue other than p.Arg138. Knowledge of the complete spectrum of dominant-acting mutations that cause this rare syndrome will have implications for molecular diagnosis and genetic counselling of these families.

Publication types

  • Case Reports

MeSH terms

  • Aldehyde Dehydrogenase / genetics*
  • Child
  • Cutis Laxa / genetics*
  • Cutis Laxa / pathology
  • Genetic Counseling
  • Genetic Predisposition to Disease*
  • Humans
  • Male
  • Mutation

Substances

  • ALDH18A1 protein, human
  • Aldehyde Dehydrogenase

Supplementary concepts

  • Cutis Laxa, Autosomal Dominant