Letter to the Editors: Concerning "Divergent clinical outcomes of alphaglucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state" by Takashi M et al

Mol Genet Metab Rep. 2017 Mar 7:11:1. doi: 10.1016/j.ymgmr.2017.02.003. eCollection 2017 Jun.
No abstract available