A Critical Review of Validation, Blind Testing, and Real- World Use of Alchemical Protein-Ligand Binding Free Energy Calculations

Curr Top Med Chem. 2017;17(23):2577-2585. doi: 10.2174/1568026617666170414142131.

Abstract

Protein-ligand binding is among the most fundamental phenomena underlying all molecular biology, and a greater ability to more accurately and robustly predict the binding free energy of a small molecule ligand for its cognate protein is expected to have vast consequences for improving the efficiency of pharmaceutical drug discovery. We briefly reviewed a number of scientific and technical advances that have enabled alchemical free energy calculations to recently emerge as a preferred approach, and critically considered proper validation and effective use of these techniques. In particular, we characterized a selection bias effect which may be important in prospective free energy calculations, and introduced a strategy to improve the accuracy of the free energy predictions.

Keywords: Alchemical free energy calculations; Computer-aided drug design; Drug discovery; FEP; Free energy; Molecular dynamics; Protein-ligand binding; Structure-based drug discovery; TI; Thermodynamic integration.

Publication types

  • Review

MeSH terms

  • Binding Sites / drug effects
  • Drug Discovery
  • Ligands
  • Proteins / antagonists & inhibitors
  • Proteins / chemistry*
  • Small Molecule Libraries / chemistry*
  • Small Molecule Libraries / pharmacology
  • Thermodynamics*

Substances

  • Ligands
  • Proteins
  • Small Molecule Libraries