An unusual genomic variant of pancreatic ductal adenocarcinoma with an indolent clinical course

Cold Spring Harb Mol Case Stud. 2017 Jul 5;3(4):a001701. doi: 10.1101/mcs.a001701. Print 2017 Jul.

Abstract

We describe an 85-yr-old male of Ashkenazi Jewish descent with biopsy-proven locally advanced pancreatic ductal adenocarcinoma (PDA). The patient underwent a modified course of gemcitabine and stereotactic body radiation therapy and survived for 42 mo with a stable pancreatic head mass and no evidence of metastatic disease before death due to complications from a stroke. Whole-exome sequencing of his tumor revealed a simple genome landscape with no evidence of mutations, copy-number changes, or structural alterations in genes most commonly associated with PDA (i.e., KRAS, CDKN2A, TP53, or SMAD4). An analysis of his germline DNA revealed no pathogenic variants of significance. Whole-exome and whole-genome sequencing identified a somatic mutation of RNF213 and an inversion/deletion of CTNNA2 as the genetic basis of his PDA. Although PDA is classically characterized by a predictable set of mutations, these data suggest that alternate genetic paths to PDA may exist, which can be associated with a more indolent clinical course.

Keywords: neoplasm of the pancreas; pancreatic adenocarcinoma.

Publication types

  • Case Reports
  • Research Support, N.I.H., Extramural

MeSH terms

  • Adenocarcinoma / genetics
  • Adenosine Triphosphatases / genetics*
  • Adenosine Triphosphatases / metabolism
  • Aged, 80 and over
  • Carcinoma, Pancreatic Ductal / drug therapy
  • Carcinoma, Pancreatic Ductal / genetics*
  • Deoxycytidine / analogs & derivatives
  • Deoxycytidine / therapeutic use
  • Exome
  • Exome Sequencing
  • Gemcitabine
  • Genomics
  • Humans
  • INDEL Mutation / genetics
  • Mutation
  • Pancreas / metabolism
  • Pancreatic Neoplasms / drug therapy
  • Pancreatic Neoplasms / genetics
  • Ubiquitin-Protein Ligases / genetics*
  • Ubiquitin-Protein Ligases / metabolism
  • alpha Catenin / genetics*
  • alpha Catenin / metabolism

Substances

  • CTNNA2 protein, human
  • alpha Catenin
  • Deoxycytidine
  • RNF213 protein, human
  • Ubiquitin-Protein Ligases
  • Adenosine Triphosphatases
  • Gemcitabine