GBA-Associated Parkinson's Disease: Progression in a Deep Brain Stimulation Cohort

J Parkinsons Dis. 2017;7(4):635-644. doi: 10.3233/JPD-171172.

Abstract

Background: Recent evidence suggests that glucosidase beta acid (GBA) mutations predispose Parkinson's disease (PD) patients to a greater burden of cognitive impairment and non-motor symptoms. This emerging knowledge has not yet been considered in patients who have undergone deep brain stimulation (DBS); a surgery that is generally contraindicated in those with cognitive deficits.

Objective: To explore the long-term phenotypic progression of GBA-associated PD, in a DBS cohort.

Methods: Thirty-four PD patients who had undergone DBS surgery between 2002 and 2011 were included in this study; 17 patients with GBA mutations were matched to 17 non-carriers. Clinical evaluation involved the administration of four assessments: The Mattis Dementia Rating Scale was used to assess cognitive function; non-motor symptoms were assessed using the Non-Motor Symptom Assessment Scale for PD; quality of life was measured using the Parkinson's Disease Questionnaire; and motor symptoms were evaluated using part III of the Movement Disorders Society Unified Parkinson's Disease Rating Scale, in on-medication/on-stimulation conditions. Levodopa equivalent doses (LED) and DBS settings were compared with clinical outcomes.

Results: At a mean follow-up of 7.5 years after DBS, cognitive impairment was more prevalent (70% vs 19%) and more severe in GBA mutation carriers compared to non-carriers (60% vs 6% were severely impaired). Non-motor symptoms were also more severe and quality of life more impaired in GBA-associated PD. Motor symptoms, LED, and stimulation settings were not significantly different between groups at follow-up.

Conclusions: GBA status appears to be an important predictor for non-motor symptom disease progression, after deep brain stimulation surgery.

Keywords: Deep brain stimulation; Parkinson’s disease; glucosidase beta acid; phenotype.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Case-Control Studies
  • Cognition Disorders / etiology
  • Cohort Studies
  • Deep Brain Stimulation / methods*
  • Disease Progression
  • Female
  • Glucosylceramidase / genetics*
  • Humans
  • Male
  • Middle Aged
  • Mutation / genetics*
  • Neuropsychological Tests
  • Parkinson Disease / complications
  • Parkinson Disease / genetics*
  • Parkinson Disease / psychology
  • Parkinson Disease / therapy*
  • Quality of Life / psychology
  • Severity of Illness Index

Substances

  • Glucosylceramidase