A glucagon-like peptide-1 receptor agonist reduces intracranial pressure in a rat model of hydrocephalus

Sci Transl Med. 2017 Aug 23;9(404):eaan0972. doi: 10.1126/scitranslmed.aan0972.

Abstract

Current therapies for reducing raised intracranial pressure (ICP) under conditions such as idiopathic intracranial hypertension or hydrocephalus have limited efficacy and tolerability. Thus, there is a pressing need to identify alternative drugs. Glucagon-like peptide-1 receptor (GLP-1R) agonists are used to treat diabetes and promote weight loss but have also been shown to affect fluid homeostasis in the kidney. We investigated whether exendin-4, a GLP-1R agonist, is able to modulate cerebrospinal fluid (CSF) secretion at the choroid plexus and subsequently reduce ICP in rats. We used tissue sections and cell cultures to demonstrate expression of GLP-1R in the choroid plexus and its activation by exendin-4, an effect blocked by the GLP-1R antagonist exendin 9-39. Acute treatment with exendin-4 reduced Na+- and K+-dependent adenosine triphosphatase activity, a key regulator of CSF secretion, in cell cultures. Finally, we demonstrated that administration of exendin-4 to female rats with raised ICP (hydrocephalic) resulted in a GLP-1R-mediated reduction in ICP. These findings suggest that GLP-1R agonists can reduce ICP in rodents. Repurposing existing GLP-1R agonist drugs may be a useful therapeutic strategy for treating raised ICP.

MeSH terms

  • Animals
  • Choroid Plexus / drug effects
  • Choroid Plexus / metabolism
  • Consciousness / drug effects
  • Cyclic AMP / metabolism
  • Disease Models, Animal
  • Exenatide
  • Female
  • Glucagon-Like Peptide-1 Receptor / agonists*
  • Glucagon-Like Peptide-1 Receptor / metabolism
  • Humans
  • Hydrocephalus / drug therapy*
  • Hydrocephalus / physiopathology*
  • Intracranial Pressure* / drug effects
  • Peptides / pharmacology
  • Peptides / therapeutic use*
  • Postmortem Changes
  • RNA, Messenger / genetics
  • RNA, Messenger / metabolism
  • Rats, Sprague-Dawley
  • Sodium-Potassium-Exchanging ATPase / metabolism
  • Venoms / pharmacology
  • Venoms / therapeutic use*

Substances

  • Glucagon-Like Peptide-1 Receptor
  • Peptides
  • RNA, Messenger
  • Venoms
  • Exenatide
  • Cyclic AMP
  • Sodium-Potassium-Exchanging ATPase