De novo Mutation in CACNA1S Gene in a 20-Year-Old Man Diagnosed with Metabolic Myopathy

Arch Iran Med. 2017 Sep;20(9):617-620.

Abstract

The calcium channel, voltage-dependent, L-type, alpha 1S subunit (CACNA1S) gene encodes a skeletal Ca2+ channel which is involved in calcium-dependent processes such as muscle contraction and neurotransmitter release. Mutations in this gene have been accompanied by hypo- and normokalemic periodic paralysis, thyrotoxic periodic paralysis, and susceptibility to malignant hyperthermia. We report the clinical and genetic findings in a patient diagnosed with metabolic myopathy who had episodic attacks of muscle pain and weakness but with no family background of the disease. Next-generation sequencing (NGS) using a panel targeting metabolic myopathy and myotonia genes identified a de novo heterozygous pathogenic variant c.3724A>G, p.Arg1242Gly, in exon 30 of CACNA1S. As the second report of this variant, this case may broaden the CACNA1S-related disease spectrum to include normokalemic periodic paralysis.

Publication types

  • Case Reports

MeSH terms

  • Calcium Channels / genetics*
  • Calcium Channels, L-Type
  • Creatine Kinase / blood
  • DNA Mutational Analysis
  • Exome Sequencing
  • Humans
  • Male
  • Muscular Diseases / genetics*
  • Mutation
  • Young Adult

Substances

  • CACNA1S protein, human
  • Calcium Channels
  • Calcium Channels, L-Type
  • Creatine Kinase