Clinical course, therapeutic responses and outcomes in relapsing MOG antibody-associated demyelination

J Neurol Neurosurg Psychiatry. 2018 Feb;89(2):127-137. doi: 10.1136/jnnp-2017-316880. Epub 2017 Nov 15.

Abstract

Objective: We characterised the clinical course, treatment and outcomes in 59 patients with relapsing myelin oligodendrocyte glycoprotein (MOG) antibody-associated demyelination.

Methods: We evaluated clinical phenotypes, annualised relapse rates (ARR) prior and on immunotherapy and Expanded Disability Status Scale (EDSS), in 218 demyelinating episodes from 33 paediatric and 26 adult patients.

Results: The most common initial presentation in the cohort was optic neuritis (ON) in 54% (bilateral (BON) 32%, unilateral (UON) 22%), followed by acute disseminated encephalomyelitis (ADEM) (20%), which occurred exclusively in children. ON was the dominant phenotype (UON 35%, BON 19%) of all clinical episodes. 109/226 (48%) MRIs had no brain lesions. Patients were steroid responsive, but 70% of episodes treated with oral prednisone relapsed, particularly at doses <10 mg daily or within 2 months of cessation. Immunotherapy, including maintenance prednisone (P=0.0004), intravenous immunoglobulin, rituximab and mycophenolate, all reduced median ARRs on-treatment. Treatment failure rates were lower in patients on maintenance steroids (5%) compared with non-steroidal maintenance immunotherapy (38%) (P=0.016). 58% of patients experienced residual disability (average follow-up 61 months, visual loss in 24%). Patients with ON were less likely to have sustained disability defined by a final EDSS of ≥2 (OR 0.15, P=0.032), while those who had any myelitis were more likely to have sustained residual deficits (OR 3.56, P=0.077).

Conclusion: Relapsing MOG antibody-associated demyelination is strongly associated with ON across all age groups and ADEM in children. Patients are highly responsive to steroids, but vulnerable to relapse on steroid reduction and cessation.

Keywords: acute disseminated encephalomyelitis; myelin oligodendrocyte glycoprotein antibodies; optic neuritis; outcomes; therapy.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Autoantibodies / immunology
  • Brain / diagnostic imaging
  • Child
  • Child, Preschool
  • Cohort Studies
  • Demyelinating Autoimmune Diseases, CNS / diagnostic imaging
  • Demyelinating Autoimmune Diseases, CNS / immunology
  • Demyelinating Autoimmune Diseases, CNS / physiopathology
  • Demyelinating Autoimmune Diseases, CNS / therapy*
  • Encephalomyelitis, Acute Disseminated / diagnostic imaging
  • Encephalomyelitis, Acute Disseminated / immunology
  • Encephalomyelitis, Acute Disseminated / physiopathology
  • Encephalomyelitis, Acute Disseminated / therapy
  • Female
  • Humans
  • Immunoglobulins, Intravenous / therapeutic use
  • Immunologic Factors / therapeutic use
  • Immunosuppressive Agents / therapeutic use*
  • Immunotherapy
  • Infant
  • Magnetic Resonance Imaging
  • Male
  • Middle Aged
  • Mycophenolic Acid / therapeutic use
  • Myelin-Oligodendrocyte Glycoprotein / immunology
  • Myelitis, Transverse / diagnostic imaging
  • Myelitis, Transverse / immunology
  • Myelitis, Transverse / physiopathology
  • Myelitis, Transverse / therapy
  • Neuromyelitis Optica / diagnostic imaging
  • Neuromyelitis Optica / immunology
  • Neuromyelitis Optica / physiopathology
  • Neuromyelitis Optica / therapy
  • Optic Neuritis / diagnostic imaging
  • Optic Neuritis / immunology
  • Optic Neuritis / physiopathology
  • Optic Neuritis / therapy
  • Prednisone / therapeutic use
  • Rituximab / therapeutic use
  • Young Adult

Substances

  • Autoantibodies
  • Immunoglobulins, Intravenous
  • Immunologic Factors
  • Immunosuppressive Agents
  • Myelin-Oligodendrocyte Glycoprotein
  • Rituximab
  • Mycophenolic Acid
  • Prednisone