A Bispecific Antibody Based on Pertuzumab Fab Has Potent Antitumor Activity

J Immunother. 2018 Jan;41(1):1-8. doi: 10.1097/CJI.0000000000000200.

Abstract

Human epidermal growth factor receptor 2 (HER2) is frequently overexpressed and activated in metastatic breast cancers. Monoclonal antibodies targeting Her2, such as trastuzumab and pertuzumab, have become important targeted therapies for patients with HER2-positive breast cancer. Both trastuzumab and pertuzumab can reduce Her2 positive tumor burden by inhibiting Her2 signaling and inducing ADCC activities (antibody dependent cell-mediated cytotoxicity). In this study, we have generated a bispecific antibody, Her2(Per)-S-Fab, by linking the pertuzumab Fab to an anti-CD16 single domain antibody. The Her2(Per)-S-Fab can be expressed and purified efficiently from Escherichia coli. In vitro and in vivo experiments showed Her2(Per)-S-Fab had potent cytotoxicity against Her2-positive tumor cells. Thus, Her2(Per)-S-Fab may provide an alternative to treat Her2-positive cancer patients.

MeSH terms

  • Animals
  • Antibodies, Bispecific / genetics*
  • Antibodies, Bispecific / therapeutic use
  • Antibodies, Monoclonal, Humanized / genetics
  • Antibodies, Monoclonal, Humanized / therapeutic use*
  • Antibody-Dependent Cell Cytotoxicity
  • Antineoplastic Combined Chemotherapy Protocols / therapeutic use*
  • Breast Neoplasms / immunology
  • Breast Neoplasms / therapy*
  • Escherichia coli / genetics
  • Female
  • Gene Expression Regulation, Neoplastic
  • Humans
  • Immunotherapy / methods*
  • MCF-7 Cells
  • Mice
  • Mice, SCID
  • Molecular Targeted Therapy
  • Neoplasm Metastasis
  • Protein Engineering
  • Receptor, ErbB-2 / genetics*
  • Receptor, ErbB-2 / immunology
  • Receptor, ErbB-2 / metabolism
  • Receptors, IgG / immunology
  • Signal Transduction
  • Single-Domain Antibodies / genetics
  • Single-Domain Antibodies / therapeutic use
  • Trastuzumab / therapeutic use
  • Tumor Burden
  • Xenograft Model Antitumor Assays

Substances

  • Antibodies, Bispecific
  • Antibodies, Monoclonal, Humanized
  • Receptors, IgG
  • Single-Domain Antibodies
  • ERBB2 protein, human
  • Receptor, ErbB-2
  • pertuzumab
  • Trastuzumab