Structural basis of membrane disruption and cellular toxicity by α-synuclein oligomers

Science. 2017 Dec 15;358(6369):1440-1443. doi: 10.1126/science.aan6160.

Abstract

Oligomeric species populated during the aggregation process of α-synuclein have been linked to neuronal impairment in Parkinson's disease and related neurodegenerative disorders. By using solution and solid-state nuclear magnetic resonance techniques in conjunction with other structural methods, we identified the fundamental characteristics that enable toxic α-synuclein oligomers to perturb biological membranes and disrupt cellular function; these include a highly lipophilic element that promotes strong membrane interactions and a structured region that inserts into lipid bilayers and disrupts their integrity. In support of these conclusions, mutations that target the region that promotes strong membrane interactions by α-synuclein oligomers suppressed their toxicity in neuroblastoma cells and primary cortical neurons.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cell Line, Tumor
  • Cell Membrane / chemistry
  • Cerebral Cortex / chemistry
  • Humans
  • Lipid Bilayers
  • Mutation
  • Neurons / chemistry
  • Neurons / drug effects
  • Nuclear Magnetic Resonance, Biomolecular
  • Parkinson Disease / metabolism*
  • Protein Aggregation, Pathological / metabolism*
  • alpha-Synuclein / chemistry*
  • alpha-Synuclein / genetics
  • alpha-Synuclein / toxicity*

Substances

  • Lipid Bilayers
  • alpha-Synuclein