Identification of Hsp90 Inhibitors with Anti-Plasmodium Activity

Antimicrob Agents Chemother. 2018 Mar 27;62(4):e01799-17. doi: 10.1128/AAC.01799-17. Print 2018 Apr.

Abstract

Malaria remains a global health burden partly due to Plasmodium parasite resistance to first-line therapeutics. The molecular chaperone heat shock protein 90 (Hsp90) has emerged as an essential protein for blood-stage Plasmodium parasites, but details about its function during malaria's elusive liver stage are unclear. We used target-based screens to identify compounds that bind to Plasmodium falciparum and human Hsp90, which revealed insights into chemotypes with species-selective binding. Using cell-based malaria assays, we demonstrate that all identified Hsp90-binding compounds are liver- and blood-stage Plasmodium inhibitors. Additionally, the Hsp90 inhibitor SNX-0723 in combination with the phosphatidylinositol 3-kinase inhibitor PIK-75 synergistically reduces the liver-stage parasite load. Time course inhibition studies with the Hsp90 inhibitors and expression analysis support a role for Plasmodium Hsp90 in late-liver-stage parasite development. Our results suggest that Plasmodium Hsp90 is essential to liver- and blood-stage parasite infections and highlight an attractive route for development of species-selective PfHsp90 inhibitors that may act synergistically in combination therapies to prevent and treat malaria.

Keywords: Hsp90; Plasmodium; host-pathogen interaction; malaria.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antimalarials / therapeutic use*
  • Benzamides / therapeutic use
  • HSP90 Heat-Shock Proteins / antagonists & inhibitors*
  • HSP90 Heat-Shock Proteins / metabolism
  • Host-Pathogen Interactions
  • Humans
  • Hydrazones / therapeutic use
  • Indoles / therapeutic use
  • Malaria / drug therapy
  • Malaria / metabolism
  • Plasmodium falciparum / drug effects
  • Plasmodium falciparum / metabolism
  • Plasmodium falciparum / pathogenicity
  • Sulfonamides / therapeutic use
  • ortho-Aminobenzoates / therapeutic use

Substances

  • 2-fluoro-6-(tetrahydrofuran-3-ylamino)-4-(3,6,6-trimethyl-4-oxo-4,5,6,7-tetrahydro-1H-indol-1-yl)benzamide
  • Antimalarials
  • Benzamides
  • HSP90 Heat-Shock Proteins
  • Hydrazones
  • Indoles
  • PIK 75
  • Sulfonamides
  • ortho-Aminobenzoates