1 Division of Hematopoietic Innovative Therapies, Centro de Investigaciones Energéticas Medioambientales y Tecnológicas (CIEMAT) and Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER-ISCIII), Madrid, Spain; Advanced Therapies Unit, Instituto de Investigación Sanitaria Fundación Jiménez Díaz (IIS-FJD/UAM), Madrid, Spain.
2 Rocket Pharmaceuticals, New York, NY. Electronic address: [email protected].
3 Institute of Child Health, Molecular and Cellular Immunology, University College London, Great Ormond Street Institute of Child Health, London, United Kingdom.
4 University of California Los Angeles, Los Angeles, Calif.