A novel variant in ATM gene causes ataxia telangiectasia revealed by whole-exome sequencing

Neurosciences (Riyadh). 2018 Apr;23(2):162-164. doi: 10.17712/nsj.2018.2.20170463.

Abstract

Ataxia-Telangiectasia (A-T) is an autosomal recessive disorder caused by variants in ATM gene and characterized by progressive neurologic impairment, cerebellar ataxia, and oculo-cutaneous telangiectasia. Immunodeficiency with a recurrent sinopulmonary infections are observed in patients with A-T. Here, we report a novel stop codon variant, c.5944 C>T (p.Gln1982*), revealed by whole-exome sequencing in a 9-year old boy. He presented with recurrent upper respiratory tract infections, failure to thrive, developmental delay, ataxic gait, and bulbar telangiectasia.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Ataxia Telangiectasia / genetics*
  • Ataxia Telangiectasia / pathology
  • Ataxia Telangiectasia Mutated Proteins / genetics*
  • Codon, Nonsense*
  • Exome Sequencing
  • Humans
  • Male

Substances

  • Codon, Nonsense
  • ATM protein, human
  • Ataxia Telangiectasia Mutated Proteins