Surgical and molecular characterization of primary and metastatic disease in a neuroendocrine tumor arising in a tailgut cyst

Cold Spring Harb Mol Case Stud. 2018 Oct 1;4(5):a003004. doi: 10.1101/mcs.a003004. Print 2018 Oct.

Abstract

Neuroendocrine tumors (NETs) arising from tailgut cysts are a rare but increasingly reported entity with gene expression profiles that may be indicative of the gastrointestinal cell of origin. We present a case report describing the unique pathological and genomic characteristics of a tailgut cyst NET that metastasized to liver. The histologic and immunohistochemical findings were consistent with a well-differentiated NET. Genomic testing indicates a germline frameshift in BRCA1 and a few somatic mutations of unknown significance. Transcriptomic analysis suggests an enteroendocrine L cell in the tailgut as a putative cell of origin. Genomic profiling of a rare NET and metastasis provides insight into its origin, development, and potential therapeutic options.

Keywords: neoplasm of the gastrointestinal tract; neuroendocrine neoplasm.

Publication types

  • Case Reports
  • Research Support, N.I.H., Extramural
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Aged
  • BRCA1 Protein / genetics
  • Carcinoid Tumor
  • Cysts / metabolism
  • Hamartoma / genetics*
  • Hamartoma / pathology*
  • Humans
  • Liver / pathology
  • Liver Neoplasms / metabolism
  • Male
  • Neoplasm Metastasis / pathology
  • Neuroendocrine Tumors / genetics
  • Neuroendocrine Tumors / pathology
  • Sacrococcygeal Region / pathology

Substances

  • BRCA1 Protein
  • BRCA1 protein, human