Effects of amino acid substitutions on the biological activity of anti-CD20 monoclonal antibody produced by transgenic silkworms (Bombyx mori)

Biochem Biophys Res Commun. 2018 Sep 18;503(4):2633-2638. doi: 10.1016/j.bbrc.2018.08.015. Epub 2018 Aug 14.

Abstract

Recombinant monoclonal antibodies (mAbs) have been used in various therapeutic applications including cancer therapy. Fc-mediated effector functions play a pivotal role in the tumor-killing activities of some tumor-targeting mAbs, and Fc-engineering technologies with glyco-engineering or amino acid substitutions at the antibody Fc region have been used to enhance cytotoxic activities including antibody-dependent cellular cytotoxicity (ADCC). We previously reported that the mAbs produced using transgenic silkworms showed stronger ADCC activity and lower complement-dependent cytotoxicity (CDC) activity than mAbs derived from Chinese hamster ovary (CHO) cells due to their unique N-glycan structure (lack of core-fucose and non-reducing terminal galactose). In this study, we generated anti-CD20 mAbs with amino acid substitutions using transgenic silkworms and analyzed their biological activities to assess the effect of the combination of glyco-engineering and amino acid substitutions on the Fc-mediated function of mAbs. Three types of amino acid substitutions at the Fc region (G236A/S239D/I332E, L234A/L235A, and K326W/E333S) modified the Fc-mediated biological activities of silkworm-derived mAbs as in the case of CHO-derived mAbs, resulting in the generation of Fc-engineered mAbs with characteristic Fc-mediated functions. The combination of amino acid substitutions at the Fc region and glyco-engineering using transgenic silkworm made it possible to generate Fc-engineered mAbs with suitable Fc-mediated biological functions depending on the pharmacological mechanism of their actions. Transgenic silkworms were shown to be a promising system for the production of Fc-engineered mAbs.

Keywords: Amino acid substitution; Fc-mediated effector function; Monoclonal antibody; N-glycosylation; Transgenic silkworm.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Substitution
  • Animals
  • Animals, Genetically Modified
  • Antibodies, Monoclonal, Humanized / biosynthesis
  • Antibodies, Monoclonal, Humanized / chemistry*
  • Antibodies, Monoclonal, Humanized / genetics
  • Antibody-Dependent Cell Cytotoxicity*
  • Antigens, CD20 / genetics
  • Antigens, CD20 / immunology*
  • Bombyx / genetics*
  • Carbohydrate Sequence
  • Cell Line, Tumor
  • Fucose / chemistry
  • Fucose / immunology
  • Galactose / chemistry
  • Galactose / immunology
  • Gene Expression
  • Humans
  • Immunoglobulin Fc Fragments / biosynthesis
  • Immunoglobulin Fc Fragments / chemistry*
  • Immunoglobulin Fc Fragments / genetics
  • Jurkat Cells
  • Lymphocytes / cytology
  • Lymphocytes / immunology*
  • Polysaccharides / chemistry
  • Polysaccharides / immunology
  • Protein Engineering

Substances

  • Antibodies, Monoclonal, Humanized
  • Antigens, CD20
  • Immunoglobulin Fc Fragments
  • Polysaccharides
  • Fucose
  • Galactose