Harnessing the power of the patient perspective for rare disease therapeutics
Neurology
.
2018 Sep 25;91(13):585-586.
doi: 10.1212/WNL.0000000000006230.
Epub 2018 Aug 24.
Authors
Kathryn J Swoboda
1
,
Flavia C Nery
2
Affiliations
1
From the Center for Human Genomics, Massachusetts General Hospital Department of Neurology, Boston.
[email protected]
.
2
From the Center for Human Genomics, Massachusetts General Hospital Department of Neurology, Boston.
PMID:
30143562
DOI:
10.1212/WNL.0000000000006230
No abstract available
Publication types
Editorial
Comment
MeSH terms
Humans
Muscular Atrophy, Spinal*
Patient Reported Outcome Measures
Rare Diseases*