Understanding Molecular Drivers of Melanin Binding To Support Rational Design of Small Molecule Ophthalmic Drugs

J Med Chem. 2018 Nov 21;61(22):10106-10115. doi: 10.1021/acs.jmedchem.8b01281. Epub 2018 Nov 13.

Abstract

Binding of drugs to ocular melanin is a prominent biological phenomenon that affects the local pharmacokinetics and pharmacodynamics in the eye. In this work, we report on the development of in vitro and in silico tools for an early assessment and prediction of melanin binding properties of small molecules. A robust high-throughput assay has been established to study the binding of large sets of compounds to melanin. The extremely randomized trees approach was used to develop an in silico model able to predict the extent of melanin binding from the molecular properties of the compounds. After the last iteration of the model, strong melanin binders could prospectively be identified with 91% accuracy. On the basis of in vitro data generated for approximately 3400 chemically diverse drug-like small molecules, pronounced correlations were observed between the extent of melanin binding and the basicity, lipophilicity, and aromaticity of the compounds.

MeSH terms

  • Chemical Phenomena
  • Computer Simulation
  • Drug Design*
  • Drug Evaluation, Preclinical
  • Melanins / metabolism*
  • Ophthalmology
  • Small Molecule Libraries / chemistry
  • Small Molecule Libraries / metabolism*
  • Small Molecule Libraries / pharmacology

Substances

  • Melanins
  • Small Molecule Libraries