Potent Metabolic Sialylation Inhibitors Based on C-5-Modified Fluorinated Sialic Acids

J Med Chem. 2019 Jan 24;62(2):1014-1021. doi: 10.1021/acs.jmedchem.8b01757. Epub 2018 Dec 31.

Abstract

Sialic acid sugars on mammalian cells regulate numerous biological processes, while aberrant expression of sialic acid is associated with diseases such as cancer and pathogenic infection. Inhibition of the sialic acid biosynthesis may therefore hold considerable therapeutic potential. To effectively decrease the sialic acid expression, we synthesized C-5-modified 3-fluoro sialic acid sialyltransferase inhibitors. We found that C-5 carbamates significantly enhanced and prolonged the inhibitory activity in multiple mouse and human cell lines. As an underlying mechanism, we have identified that carbamate-modified 3-fluoro sialic acid inhibitors are more efficiently metabolized to their active cytidine monophosphate analogues, reaching higher effective inhibitor concentrations inside cells.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amides / chemistry
  • Animals
  • Carbamates / chemistry
  • Carbon / chemistry
  • Cell Line
  • Cytidine Monophosphate / analogs & derivatives
  • Cytidine Monophosphate / metabolism
  • Halogenation
  • Humans
  • Mice
  • Sialic Acids / chemistry*
  • Sialic Acids / metabolism
  • Sialic Acids / pharmacology
  • Sialyltransferases / antagonists & inhibitors*
  • Sialyltransferases / metabolism

Substances

  • Amides
  • Carbamates
  • Sialic Acids
  • Carbon
  • Sialyltransferases
  • Cytidine Monophosphate