Defining orphan conditions in the context of the European orphan regulation: challenges and evolution

Nat Rev Drug Discov. 2019 Jul;18(7):479-480. doi: 10.1038/nrd.2018.128.
No abstract available

MeSH terms

  • Drug Development / methods*
  • European Union
  • Government Regulation
  • Humans
  • Legislation, Drug*
  • Orphan Drug Production / legislation & jurisprudence*
  • Orphan Drug Production / methods
  • Rare Diseases* / diagnosis
  • Rare Diseases* / drug therapy