Long-term Clinical Effectiveness of Ustekinumab in Patients with Crohn's Disease Who Failed Biologic Therapies: A National Cohort Study

J Crohns Colitis. 2019 Oct 28;13(11):1401-1409. doi: 10.1093/ecco-jcc/jjz080.

Abstract

Background: Ustekinumab [UST] was recently approved in Europe for the treatment of moderate to severe Crohn's disease [CD]. Long-term real-world data are currently scarce for CD patients previously exposed to several biologics.

Methods: This is an observational, national, retrospective multicentre study. Patients received intravenous UST ~6 mg/kg at baseline, with 90 mg subcutaneously thereafter every 8 weeks. Response and remission rates were assessed at Weeks 8, 16, and 52.

Results: Data from 152 patients were analysed. All patients were exposed to at least one anti-TNFα agent, with 69.7% were exposed to even two anti-TNFα and vedolizumab. After 1 year, 42.1% and 25.7% of patients had experienced clinical response and clinical remission, respectively, and 38.8% and 24.3% had achieved steroid-free clinical response and remission, respectively; 38.8% of patients discontinued therapy during the 12 months of follow-up. Colonic location was predictive of clinical response at 1 year, and low body mass index [BMI] at baseline was a negative predictor of clinical remission. Resolution of arthralgia was associated with clinical response over time. De novo arthralgia was reported by 17.9% of patients at Week 8 and 13.5% of patients at Week 52. No impact of UST on arthralgia was observed in patients with concomitant ankylosing spondylitis [n = 17]. Others adverse events were reported in 7.2% of patients.

Conclusions: This real-world cohort study confirms the effectiveness of UST in CD patients previously exposed to several biologics. Ustekinumab was well tolerated with respect to adverse events.

Podcast: This article has an associated podcast which can be accessed at https://academic.oup.com/ecco-jcc/pages/podcast.

Keywords: Clinical effectiveness; Crohn’s disease; real-life cohort; ustekinumab.

Publication types

  • Multicenter Study
  • Observational Study

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Arthralgia / drug therapy
  • Arthralgia / epidemiology
  • Belgium / epidemiology
  • Biological Therapy / adverse effects
  • Body Mass Index
  • Child
  • Cohort Studies
  • Crohn Disease / drug therapy*
  • Female
  • Gastrointestinal Agents / therapeutic use*
  • Glucocorticoids / therapeutic use
  • Humans
  • Male
  • Middle Aged
  • Remission Induction*
  • Retrospective Studies
  • Tumor Necrosis Factor-alpha / antagonists & inhibitors
  • Ustekinumab / therapeutic use*
  • Young Adult

Substances

  • Gastrointestinal Agents
  • Glucocorticoids
  • Tumor Necrosis Factor-alpha
  • Ustekinumab