Patients with SMARCA4-deficient thoracic sarcoma and severe skeletal-related events

Lung Cancer. 2019 Jun:132:59-64. doi: 10.1016/j.lungcan.2019.03.029. Epub 2019 Apr 8.

Abstract

Objectives: SMARCA4-deficient thoracic sarcoma(DTS) is a recently identified new entity of thoracic malignancies characterized by inactivation of SMARCA4. Patients with SMARCA4-DTS have a particulary aggresive clinical course and no effective treatments. However, the detailed clinical features of SMARCA4-DTS remain unclear. Here, we report the clinical courses and molecular profiles of two cases of SMARCA4-DTS.

Materials and methods: We experienced strikingly similar two patients of SMARCA4-DTS. The clinicopathologic features were reviewed, and detailed immunohistochemical and comprehensive cancer panel analysis with next generation sequencing confirmed the diagnosis.

Results: Our cases had many clinical and radiological observations characteristic of SMARCA4-DTS in common. Immunohistochemical staing showed complete loss of SMARCA4 in tumor cells. Loss of function mutations were detected in SMARCA4. We found that severe SREs comprise a new significant clinical feature of SMARCA4-DTS.

Conclusion: Integrated clinico-radiologic-pathologic-genetic diagnosis is essential for SMARCA4-DTS and physicians should pay attention to severe SREs during the clinical course of this disease.

Keywords: Lung cancer; SMARCA4; SWI/SNF complex; Skeletal related event.

Publication types

  • Case Reports

MeSH terms

  • Biomarkers, Tumor / genetics
  • Bone Diseases / diagnosis*
  • Bone Diseases / genetics
  • Bone Diseases / pathology
  • Bone and Bones / diagnostic imaging
  • Bone and Bones / pathology*
  • DNA Helicases / genetics*
  • DNA Helicases / metabolism
  • High-Throughput Nucleotide Sequencing
  • Humans
  • Immunohistochemistry
  • Lung / diagnostic imaging
  • Lung / pathology*
  • Male
  • Middle Aged
  • Mutation / genetics*
  • Nuclear Proteins / genetics*
  • Nuclear Proteins / metabolism
  • Prognosis
  • Sarcoma / diagnosis*
  • Sarcoma / genetics
  • Sarcoma / pathology
  • Thoracic Neoplasms / diagnosis*
  • Thoracic Neoplasms / genetics
  • Thoracic Neoplasms / pathology
  • Transcription Factors / genetics*
  • Transcription Factors / metabolism

Substances

  • Biomarkers, Tumor
  • Nuclear Proteins
  • Transcription Factors
  • SMARCA4 protein, human
  • DNA Helicases