Intravenous administration of cardiac progenitor cell-derived exosomes protects against doxorubicin/trastuzumab-induced cardiac toxicity

Cardiovasc Res. 2020 Feb 1;116(2):383-392. doi: 10.1093/cvr/cvz108.

Abstract

Aims: Combined administration of anthracyclines (e.g. doxorubicin; Dox) and trastuzumab (Trz), a humanized anti-human epidermal growth factor receptor 2 (HER2; ErbB2), is an effective treatment for HER2-positive breast cancer. However, both agents are associated with cardiac toxicity. Human cardiac-resident mesenchymal progenitor cells (CPCs) secrete extracellular vesicles including nanosized exosomes which protect against myocardial ischaemia. Here, we investigated the effects of these exosomes using a novel model of Dox/Trz-mediated cardiotoxicity.

Methods and results: CPCs were derived from cardiac atrial appendage specimens from patients who underwent heart surgery for heart valve disease and/or ischaemic heart disease, and exosomes were purified from CPC conditioned media. Proteomics analyses revealed that CPC exosomes contained multiple proteins involved in redox processes. Dox/Trz induced a significant increase in reactive oxygen species (ROS) in rat cardiomyocytes, which was prevented by CPC exosomes. In vivo, rats received six doses of Dox (Days 1-11), followed by six doses of Trz (Days 19-28). Three doses of either exosomes or exosome suspension vehicle were injected intravenously on Days 5, 11, and 19 in the treatment and control groups, respectively. Dox/Trz induced myocardial fibrosis, CD68+ inflammatory cell infiltrates, inducible nitric oxide synthase expression, and left ventricular dysfunction. CPC exosomes prevented these effects. These vesicles were highly enriched in miR-146a-5p compared with human dermal fibroblast exosomes. Dox upregulated Traf6 and Mpo, two known miR-146a-5p target genes (which encode signalling mediators of inflammatory and cell death axes) in myocytes. CPC exosomes suppressed miR-146a-5p target genes Traf6, Smad4, Irak1, Nox4, and Mpo in Dox-treated cells. Specific silencing of miR-146a-5p abrogated exosome-mediated suppression of those genes leading to an increase in Dox-induced cell death.

Conclusions: Human CPC exosomes attenuate Dox-/Trz-induced oxidative stress in cardiomyocytes. Systemic administration of these vesicles prevents Dox/Trz cardiotoxicity in vivo. miR-146a-5p mediates some of the benefits of exosomes in this setting.

Keywords: Anthracyclines; Cardiotoxicity; Doxorubicin; Exosomes; Trastuzumab.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Administration, Intravenous
  • Aged
  • Animals
  • Animals, Newborn
  • Cardiomyopathies / chemically induced
  • Cardiomyopathies / metabolism
  • Cardiomyopathies / physiopathology
  • Cardiomyopathies / prevention & control*
  • Cells, Cultured
  • Disease Models, Animal
  • Doxorubicin*
  • Exosomes / metabolism
  • Exosomes / transplantation*
  • Female
  • Fibrosis
  • Humans
  • Inflammation Mediators / metabolism
  • Male
  • Mesenchymal Stem Cell Transplantation*
  • MicroRNAs / genetics
  • MicroRNAs / metabolism
  • Middle Aged
  • Myocardium / metabolism
  • Myocardium / pathology*
  • Nitric Oxide Synthase Type II / metabolism
  • Rats, Sprague-Dawley
  • Rats, Wistar
  • Reactive Oxygen Species / metabolism
  • Signal Transduction
  • Trastuzumab*
  • Ventricular Dysfunction, Left / chemically induced
  • Ventricular Dysfunction, Left / metabolism
  • Ventricular Dysfunction, Left / physiopathology
  • Ventricular Dysfunction, Left / prevention & control*
  • Ventricular Function, Left
  • Ventricular Remodeling

Substances

  • Inflammation Mediators
  • MIRN146 microRNA, rat
  • MicroRNAs
  • Reactive Oxygen Species
  • Doxorubicin
  • Nitric Oxide Synthase Type II
  • Nos2 protein, rat
  • Trastuzumab