Topological control of cytokine receptor signaling induces differential effects in hematopoiesis

Science. 2019 May 24;364(6442):eaav7532. doi: 10.1126/science.aav7532. Epub 2019 May 23.

Abstract

Although tunable signaling by G protein-coupled receptors can be exploited through medicinal chemistry, a comparable pharmacological approach has been lacking for the modulation of signaling through dimeric receptors, such as those for cytokines. We present a strategy to modulate cytokine receptor signaling output by use of a series of designed C2-symmetric cytokine mimetics, based on the designed ankyrin repeat protein (DARPin) scaffold, that can systematically control erythropoietin receptor (EpoR) dimerization orientation and distance between monomers. We sampled a range of EpoR geometries by varying intermonomer angle and distance, corroborated by several ligand-EpoR complex crystal structures. Across the range, we observed full, partial, and biased agonism as well as stage-selective effects on hematopoiesis. This surrogate ligand strategy opens access to pharmacological modulation of therapeutically important cytokine and growth factor receptor systems.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Ankyrin Repeat*
  • Biomimetic Materials / pharmacology*
  • Cell Line
  • Cytokines / metabolism
  • Hematopoiesis / drug effects*
  • Humans
  • Ligands
  • Protein Engineering / methods*
  • Protein Multimerization
  • Receptors, Cytokine / chemistry
  • Receptors, Cytokine / metabolism*
  • Receptors, Erythropoietin / chemistry
  • Receptors, Erythropoietin / genetics
  • Receptors, Erythropoietin / metabolism*
  • Signal Transduction

Substances

  • Cytokines
  • Ligands
  • Receptors, Cytokine
  • Receptors, Erythropoietin