Development of an inhibitor in a child with severe hemophilia B: treatment with immunosuppression and an extended desensitization protocol

Blood Coagul Fibrinolysis. 2019 Sep;30(6):291-294. doi: 10.1097/MBC.0000000000000829.

Abstract

: Development of neutralizing alloantibodies in hemophilia B is a less common, but clinically challenging phenomenon. Novel therapeutics for hemophilia B have recently been developed and reports of clinical experience with these agents outside of clinical trials are needed. We report development of an inhibitor in a child with severe hemophilia B, and subsequent immune tolerance induction using an extended desensitization protocol with the addition of immunosuppression. This case highlights successful management of a rare complication in a rare bleeding disorder and the need for additional investigation into this infrequent and clinically challenging occurrence.

Publication types

  • Case Reports

MeSH terms

  • Child
  • Clinical Protocols
  • Factor IX / immunology
  • Hemophilia B / immunology*
  • Humans
  • Immune Tolerance
  • Immunosuppression Therapy / methods
  • Isoantibodies / biosynthesis*

Substances

  • Isoantibodies
  • Factor IX