CELA2A mutations predispose to early-onset atherosclerosis and metabolic syndrome and affect plasma insulin and platelet activation

Nat Genet. 2019 Aug;51(8):1233-1243. doi: 10.1038/s41588-019-0470-3. Epub 2019 Jul 29.

Abstract

Factors that underlie the clustering of metabolic syndrome traits are not fully known. We performed whole-exome sequence analysis in kindreds with extreme phenotypes of early-onset atherosclerosis and metabolic syndrome, and identified novel loss-of-function mutations in the gene encoding the pancreatic elastase chymotrypsin-like elastase family member 2A (CELA2A). We further show that CELA2A is a circulating enzyme that reduces platelet hyperactivation, triggers both insulin secretion and degradation, and increases insulin sensitivity. CELA2A plasma levels rise postprandially and parallel insulin levels in humans. Loss of these functions by the mutant proteins provides insight into disease mechanisms and suggests that CELA2A could be an attractive therapeutic target.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Age of Onset
  • Atherosclerosis / blood
  • Atherosclerosis / etiology
  • Atherosclerosis / pathology*
  • Case-Control Studies
  • Female
  • Genetic Predisposition to Disease
  • Humans
  • Insulin / blood*
  • Insulin Resistance
  • Islets of Langerhans / metabolism
  • Islets of Langerhans / pathology*
  • Linkage Disequilibrium
  • Male
  • Metabolic Syndrome / blood
  • Metabolic Syndrome / etiology
  • Metabolic Syndrome / pathology*
  • Middle Aged
  • Mutation*
  • Pancreatic Elastase / blood*
  • Pancreatic Elastase / genetics*
  • Pedigree
  • Platelet Activation
  • Serine Endopeptidases / genetics*

Substances

  • Insulin
  • CELA2A protein, human
  • Serine Endopeptidases
  • Pancreatic Elastase