Chemogenomic Analysis of the Druggable Kinome and Its Application to Repositioning and Lead Identification Studies

Cell Chem Biol. 2019 Nov 21;26(11):1608-1622.e6. doi: 10.1016/j.chembiol.2019.08.007. Epub 2019 Sep 11.

Abstract

Owing to the intrinsic polypharmacological nature of most small-molecule kinase inhibitors, there is a need for computational models that enable systematic exploration of the chemogenomic landscape underlying druggable kinome toward more efficient kinome-profiling strategies. We implemented VirtualKinomeProfiler, an efficient computational platform that captures distinct representations of chemical similarity space of the druggable kinome for various drug discovery endeavors. By using the computational platform, we profiled approximately 37 million compound-kinase pairs and made predictions for 151,708 compounds in terms of their repositioning and lead molecule potential, against 248 kinases simultaneously. Experimental testing with biochemical assays validated 51 of the predicted interactions, identifying 19 small-molecule inhibitors of EGFR, HCK, FLT1, and MSK1 protein kinases. The prediction model led to a 1.5-fold increase in precision and 2.8-fold decrease in false-discovery rate, when compared with traditional single-dose biochemical screening, which demonstrates its potential to drastically expedite the kinome-specific drug discovery process.

Keywords: bioassays; chemogenomic analysis; chemoinformatics; computer-aided drug discovery; drug repositioning; druggable kinome; lead screening; statistical and machine-learning model.

MeSH terms

  • Area Under Curve
  • Computer Simulation*
  • Drug Discovery
  • Drug Repositioning*
  • ErbB Receptors / antagonists & inhibitors
  • ErbB Receptors / metabolism
  • Humans
  • Protein Kinase Inhibitors / chemistry
  • Protein Kinase Inhibitors / metabolism
  • Protein Kinases / chemistry
  • Protein Kinases / metabolism
  • ROC Curve
  • Small Molecule Libraries / chemistry
  • Small Molecule Libraries / metabolism
  • Support Vector Machine
  • Vascular Endothelial Growth Factor Receptor-1 / antagonists & inhibitors
  • Vascular Endothelial Growth Factor Receptor-1 / metabolism

Substances

  • Protein Kinase Inhibitors
  • Small Molecule Libraries
  • Protein Kinases
  • EGFR protein, human
  • ErbB Receptors
  • FLT1 protein, human
  • Vascular Endothelial Growth Factor Receptor-1