Small-Molecule Inhibition of UBE2T/FANCL-Mediated Ubiquitylation in the Fanconi Anemia Pathway

ACS Chem Biol. 2019 Oct 18;14(10):2148-2154. doi: 10.1021/acschembio.9b00570. Epub 2019 Sep 23.

Abstract

The Fanconi anemia pathway orchestrates the repair of DNA interstrand cross-links and stalled replication forks. A key step in this pathway is UBE2T and FANCL-dependent monoubiquitylation of the FANCD2-FANCI complex. The Fanconi anemia pathway represents an attractive therapeutic target, because activation of this pathway has been linked to chemotherapy resistance in several cancers. However, to date, very few selective inhibitors of ubiquitin conjugation pathways are known. By using a high-throughput screen-compatible assay, we have identified a small-molecule inhibitor of UBE2T/FANCL-mediated FANCD2 monoubiquitylation that sensitizes cells to the DNA cross-linking agent, carboplatin.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cell Line, Tumor
  • Fanconi Anemia / metabolism*
  • Fanconi Anemia Complementation Group L Protein / antagonists & inhibitors*
  • Fanconi Anemia Complementation Group L Protein / metabolism
  • High-Throughput Screening Assays
  • Humans
  • Small Molecule Libraries / pharmacology*
  • Ubiquitin-Conjugating Enzymes / antagonists & inhibitors*
  • Ubiquitin-Conjugating Enzymes / metabolism
  • Ubiquitination

Substances

  • Small Molecule Libraries
  • UBE2T protein, human
  • Ubiquitin-Conjugating Enzymes
  • FANCL protein, human
  • Fanconi Anemia Complementation Group L Protein