[Genetic analysis of a pedigree affected with X-linked adrenoleukodystrophy]

Zhonghua Yi Xue Yi Chuan Xue Za Zhi. 2019 Nov 10;36(11):1104-1106. doi: 10.3760/cma.j.issn.1003-9406.2019.11.012.
[Article in Chinese]

Abstract

Objective: To explore the genetic basis for a pedigree affected with X-linked adrenoleukodystrophy presenting as spastic paraplegia of the lower limbs.

Methods: Genomic DNA was extracted from peripheral blood samples of the patient and his mother. Potential variant was detected with a panel for genes associated with spastic paraplegia. Candidate variant was verified by PCR and Sanger sequencing.

Results: Both the proband and his mother presented with walking difficulty. A previously known variant, c.623T to A (p.V208E), was identified in the ABCD1 gene mapped on chromosome X in both.

Conclusion: X-link adrenoleukodystrophy should be taken into account as a possible diagnosis for this pedigree.

MeSH terms

  • ATP Binding Cassette Transporter, Subfamily D, Member 1 / genetics*
  • Adrenoleukodystrophy / genetics*
  • Female
  • Genetic Testing
  • Humans
  • Male
  • Pedigree
  • Spastic Paraplegia, Hereditary

Substances

  • ABCD1 protein, human
  • ATP Binding Cassette Transporter, Subfamily D, Member 1