1 The Floating Hospital for Children at Tufts Medical Center and the Tufts Clinical and Translational Science Institute, Boston, MA. Electronic address: [email protected].
2 US Food and Drug Administration, Office of Pediatric Therapeutics, Silver Spring, MD.
3 Health Canada, Ottawa, Ontario, Canada.
4 Pharmaceuticals and Medical Devices Agency, Tokyo, Japan.
5 Chiesi Farmaceutici SpA, Parma, Italy.
6 Takeda Pharmaceutical Company Limited, Zug, Switzerland.
11 National Center for Child Health and Development, Tokyo, Japan.
12 Department of Development and Regeneration, KU Leuven, Leuven, Belgium.
13 Department of Development and Regeneration, KU Leuven, Leuven, Belgium; Department of Pediatrics, Division of Neonatology, Erasmus MC-Sophia Children's Hospital, Rotterdam, the Netherlands.
14 US Food and Drug Administration, Center for Drug Evaluation and Research, Silver Spring, MD.
15 Institute of Translational Medicine, University of Liverpool, Liverpool, United Kingdom.