Clinical trial data available for UX001, aceneuramic acid extended-release

J Neurol Sci. 2020 Apr 15:411:116724. doi: 10.1016/j.jns.2020.116724. Epub 2020 Feb 5.

Author

Camille L Bedrosian¹

Affiliation

¹ Ultragenyx Pharmaceutical Inc., Novato, CA, United States. Electronic address: [email protected].

PMID: 32058180
DOI: 10.1016/j.jns.2020.116724

No abstract available

Keywords: Aceneuramic acid extended-release; Glucosamine (UDP-N-acetyl)-2-epimerase myopathy; Inclusion body myopathy; Negative results.

Publication types

Letter

MeSH terms

Carbohydrate Epimerases
Distal Myopathies*
Humans
N-Acetylneuraminic Acid*

Substances

Carbohydrate Epimerases
N-Acetylneuraminic Acid