Multitarget Compounds for Bipolar Disorder: From Rational Design to Preliminary Pharmacokinetic Evaluation

ChemMedChem. 2020 Jun 4;15(11):949-954. doi: 10.1002/cmdc.202000210. Epub 2020 Apr 29.

Abstract

Due to the complex and multifactorial nature of bipolar disorder (BD), single-target drugs have traditionally provided limited relief with no disease-modifying effects. In line with the polypharmacology paradigm, we attempted to overcome these limitations by devising two series of multitarget-directed ligands endowed with both a partial agonist profile at dopamine receptor D3 (D3R) and inhibitory activity against glycogen synthase kinase 3 beta (GSK-3β). These are two structurally unrelated targets that play independent, yet connected, roles in cognition and mood regulation. Two compounds (7 and 10) emerged as promising D3R/GSK-3β multitarget-directed ligands with nanomolar activity at D3R and low-micromolar inhibition of GSK-3β, thereby confirming, albeit preliminarily, the feasibility of our strategy. Furthermore, 7 showed promising drug-like properties in stability and pharmacokinetic studies.

Keywords: drug discovery; enzymes; molecular modeling; polypharmacology; receptors.

MeSH terms

  • Antipsychotic Agents / chemical synthesis
  • Antipsychotic Agents / chemistry
  • Antipsychotic Agents / pharmacokinetics*
  • Bipolar Disorder / drug therapy*
  • Bipolar Disorder / metabolism
  • Dose-Response Relationship, Drug
  • Drug Design*
  • Glycogen Synthase Kinase 3 beta / antagonists & inhibitors
  • Glycogen Synthase Kinase 3 beta / metabolism
  • Humans
  • Molecular Structure
  • Receptors, Dopamine D3 / agonists
  • Receptors, Dopamine D3 / metabolism
  • Structure-Activity Relationship

Substances

  • Antipsychotic Agents
  • Receptors, Dopamine D3
  • Glycogen Synthase Kinase 3 beta