Prevalence of C9orf72 hexanucleotide repeat expansion in Greek patients with sporadic ALS

Amyotroph Lateral Scler Frontotemporal Degener. 2020 Aug;21(5-6):470-472. doi: 10.1080/21678421.2020.1757115. Epub 2020 Apr 26.

Abstract

A total of 178 consecutive patients with definite sALS without frontotemporal dementia (FTD) were enrolled in this study, after complete clinical evaluation. A Repeat-Primed Polymerase Chain Reaction (RP-PCR) protocol was applied to detect the G4C2 repeats expansions. In the studied sALS patients, 5.06% (n = 9) carried the C9orf72 mutation. Among carriers, 2/3 of them were females and spinal onset accounted for 78% and bulbar for 22%, while the mean age of onset was about 60 years. Our study showed that the prevalence of C9orf72 repeat expansion in Greek sALS patients is similar to the overall frequency of the mutation in European populations. The pathogenic mutation remains a promising biomarker for genetic testing and targeted treatment.

Keywords: C9orf72 expansion; Greek cohort; hexanucleotide repeats; sporadic amyotrophic lateral sclerosis.

MeSH terms

  • Amyotrophic Lateral Sclerosis* / epidemiology
  • Amyotrophic Lateral Sclerosis* / genetics
  • C9orf72 Protein / genetics
  • Cohort Studies
  • DNA Repeat Expansion / genetics
  • Female
  • Greece / epidemiology
  • Humans
  • Middle Aged
  • Prevalence
  • Proteins / genetics

Substances

  • C9orf72 Protein
  • C9orf72 protein, human
  • Proteins

Supplementary concepts

  • Amyotrophic Lateral Sclerosis 2, Juvenile