[A case of motor and sensory polyneuropathy and respiratory failure with novel heterozygous mutation of the senataxin gene]

Rinsho Shinkeigaku. 2020 Jul 31;60(7):466-472. doi: 10.5692/clinicalneurol.60.cn-001415. Epub 2020 Jun 13.
[Article in Japanese]

Abstract

The patient was a 29-year-old male. He took his first steps at two-and-a-half years old, but his physical strength deteriorated and he became non-ambulatory at 12 years old. He had respiratory failure at the age of 20, and finally underwent tracheostomy with invasive positive-pressure ventilation (TPPV). He showed distal dominant muscle weakness and atrophy, including the face. Spinal scoliosis was recognized. He had peripheral predominance of sensory disorders. Nerve conduction studies showed a decrease of compound muscle action potential and a reduction of motor nerve conduction velocity. Sensory nerve action potential was not evoked. In genetic analysis, c.23 C> T (p. T8M) heterozygous mutation was found in the senataxin gene (SETX). Although SETX is a causative gene of familial amyotrophic lateral sclerosis type 4 (ALS4), this case suggests that SETX mutation can also cause motor and sensory polyneuropathy.

Keywords: ALS4; motor and sensory polyneuropathy; respiratory failure; senataxin.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Amyotrophic Lateral Sclerosis
  • Child
  • Child, Preschool
  • DNA Helicases / genetics*
  • Heterozygote*
  • Humans
  • Male
  • Motor Neurons
  • Multifunctional Enzymes / genetics*
  • Muscle Weakness / etiology
  • Mutation*
  • Polyneuropathies / etiology*
  • Polyneuropathies / genetics*
  • RNA Helicases / genetics*
  • Respiratory Insufficiency / etiology*
  • Respiratory Insufficiency / genetics*
  • Sensory Receptor Cells

Substances

  • Multifunctional Enzymes
  • SETX protein, human
  • DNA Helicases
  • RNA Helicases

Supplementary concepts

  • Amyotrophic Lateral Sclerosis 4, Juvenile